Gene therapy is a medical technology that aims to produce a therapeutic effect through the manipulation of gene expression or through altering the biological...

Gene therapy utilizes the delivery of DNA into cells, which can be accomplished by several methods, summarized below. The two major classes of methods...

This article contains a list of commercially available gene therapies. Alipogene tiparvovec (Glybera): AAV-based treatment for lipoprotein lipase deficiency...

genes: gene therapy gene therapy for epilepsy gene therapy for osteoarthritis gene therapy for color blindness gene therapy of the human retina gene therapy...

Gene therapy for color blindness is an experimental gene therapy of the human retina aiming to grant typical trichromatic color vision to individuals with...

using gene therapy as routine therapy is not suggested. A small study published in 2015 found a small benefit. The focus of much CF gene therapy research...

and thus its host organism. Gene delivery is a necessary step in gene therapy for the introduction or silencing of a gene to promote a therapeutic outcome...

Lentiviral vectors in gene therapy is a method by which genes can be inserted, modified, or deleted in organisms using lentiviruses. Lentiviruses are...

allele in certain populations. Researchers are looking at gene therapy or enzyme replacement therapy as possible treatments. Tay–Sachs disease is typically...

Emmanuel (February 2016). "Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β – Gene". Human Gene Therapy. 27 (2): 148–165. doi:10...